[CIS PIDD] [cis-pidd] ADA-deficient SCID

Mon Mar 6 16:06:47 EST 2017

Their protocol calls for patients with ADA SCID without an HLA identical donor.

L Kobrynski

Lisa Kobrynski, MD, MPH
Associate ProfessorThey  of Pediatrics
Marcus Professor of Immunology
Section, Allergy/Immunology

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From: CIS-PIDD <cis-pidd at lists.clinimmsoc.org>
Sent: Friday, March 3, 2017 9:48 AM
To: CIS-PIDD
Subject: RE:[cis-pidd] ADA-deficient SCID

Don Kohn, UCLA

DKohn1 at mednet.ucla.edu

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From: CIS-PIDD [mailto:cis-pidd at lists.clinimmsoc.org]
Sent: Friday, March 03, 2017 9:42 AM
To: CIS-PIDD
Subject: [cis-pidd] ADA-deficient SCID

I have a new ADA deficient SCID.  Three weeks old.  Perfectly healthy. No sibs.

What are the current gene therapy options in the U.S.?

Howard

Sent from my Verizon Wireless 4G LTE DROID

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